New and Emerging Phenotypes in Lysosomal Storage Disorders
![New and Emerging Phenotypes in Lysosomal Storage Disorders](https://d3wo5wojvuv7l.cloudfront.net/t_square_limited_480/images.spreaker.com/original/127427015344045bbed44785a2d09774.jpg)
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Descrizione
Drs. Ozlem Goker-Alpan and Uma Ramaswami discuss how the success of therapies to treat lysosomal storage disorders like Pompe disease, Gaucher disease, and various MPSs, has created phenotypes that previously...
mostra di piùThis CME/CE activity is possible through an educational grant from Takeda, Cheisi, Ultragenyx Pharmaceuticals, and Spark Therapeutics.
To obtain credit for this activity, please visit https://checkrare.com/learning-center/courses/
Informazioni
Autore | Peter Ciszewski, CheckRare |
Sito | - |
Tag |
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